Amicus is the American biopharmaceutical company that is located in Cranbury, New Jersey. Amicus Therapeutics went public back in the year 2007 where they operated under the NASDAQ symbol of FOLD. This business was created by many venture capital firms which included the firm Radius Ventures(Yahoo Finance). It also worked alongside of New Enterprise Associates.
The therapeutic focus for the business is surrounding orphan and rare diseases. It works to create a plan on different therapy options for various diseases and in 2014, the business was said to have the largest portfolio for small molecules within the pharmacological chaperones within the industry of pharmaceuticals.
There are a number of diseases out there that leaves patients without hope that they can be cured or treated. A specific example is of Fabry Disease. This disease is a genetic disorder and to help people overcome the disease, the latest product of Amicus Therapeutics is Migalastat. By creating a number of enzyme replacement therapies, patients who suffer from this disease are able to see a difference in their lives.
The goal of Amicus Therapeutics is to help patients who are suffering from a disease to live longer and healthier lives by allowing therapies to work to alleviate the symptoms of various diseases. They are very passionate and the work they are doing and are always thinking of different things to do to help patients. As long as they continue to push the idea of each therapy and to take a number of risks that will push for different advances to be made, more patients are able to be helped when they suffer from a genetic disorder or disease.
The goal of the company is to think outside of the box and to keep asking the questions that are the hardest to answer. The business knows that in order to make a difference, they have to know and understand the mistakes that have been made. Once you understand a mistake and know how to avoid it, you start to learn how to avoid it and bypass it the next time. It encourages more hope and promise which is what patients need when they suffer from a disease or disorder.